Successful engraftment of gene-corrected hematopoietic stem cells in non-conditioned patients with Fanconi anemia
Paula Rı́o(Centre for Biomedical Network Research on Rare Diseases), Juan A. Bueren(Centro de Investigación Biomédica en Red), Laura Cerrato(Centre for Biomedical Network Research on Rare Diseases), Anne Galy(Centre National de la Recherche Scientifique), Raquel Hladun(Vall d'Hebron Institut de Recerca), Irina Giralt(Vall d'Hebron Institut de Recerca), Albert Català(Hospital Sant Joan de Déu Barcelona), Eva Heredero Gálvez(Hospital Municipal de Badalona), Ning Wu(Capital Medical University), Susana Navarro(Centre for Biomedical Network Research on Rare Diseases), Omaira Alberquilla(Cipher Gene (China)), Nagore García de Andoín(Biogipuzkoa Health Research Institute), Yari Giménez(Centre for Biomedical Network Research on Rare Diseases), Francisco J Roman‐Rodriguez(Centre for Biomedical Network Research on Rare Diseases), Cristina Díaz de Heredia(Universitat Autònoma de Barcelona), José C. Segovia(Unidades Centrales Científico-Técnicas), Julián Sevilla(University of Southern Denmark), Manfred Schmidt(Centre National de la Recherche Scientifique), Eva Merino(Centre for Biomedical Network Research on Rare Diseases), Jean Soulier(Centre National de la Recherche Scientifique), Miriam Hernando-Rodríguez(Centre for Biomedical Network Research on Rare Diseases), Rebeca Sánchez‐Domínguez, Rosa María Pérez Yáñez(Instituto de Salud Carlos III), José Antonio Casado(Centre for Biomedical Network Research on Rare Diseases), Rocío Salgado(Hospital Universitario Fundación Jiménez Díaz), Anna Raimbault(Délégation Paris 5), Ricardo López Almaraz(BioCruces Health research Institute), Jordi Surrallés(Universitat Autònoma de Barcelona), Jonathan D. Schwartz(Temple University), Massimo Bogliolo(Universitat Autònoma de Barcelona), Lara Álvarez(Centre for Biomedical Network Research on Rare Diseases), Wei Wang(First Affiliated Hospital of Guangzhou Medical University), Roser Pujol(Universitat Autònoma de Barcelona), M. Luz Lozano(Centre for Biomedical Network Research on Rare Diseases), Jordi Barquinero(Vall d'Hebron Institut de Recerca), María L. Lamana(Centre for Biomedical Network Research on Rare Diseases), Guillermo Güenechea(Centre for Biomedical Network Research on Rare Diseases)
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