Successful engraftment of gene-corrected hematopoietic stem cells in non-conditioned patients with Fanconi anemiaPaula Rı́o, Juan A. Bueren, Susana Navarro et al.|Nature Medicine|2019Cited by 180
Engraftment and in vivo proliferation advantage of gene-corrected mobilized CD34+ cells from Fanconi anemia patientsPaula Rı́o, Juan A. Bueren, Guillermo Güenechea et al.|Blood|2017Cited by 60
Haematopoietic gene therapy of non-conditioned patients with Fanconi anaemia-A: results from open-label phase 1/2 (FANCOLEN-1) and long-term clinical trialsPaula Rı́o, Josune Zubicaray, Susana Navarro et al.|The Lancet|2024Cited by 27
Advances in the Gene Therapy of Patients with Fanconi AnemiaJuan A. Bueren, Julián Sevilla, Susana Navarro et al.|Blood|2018Cited by 3
Hematopoietic Engraftment of Fanconi Anemia Patients through 3 Years after Gene TherapyPaula Rı́o, Juan A. Bueren, Susana Navarro et al.|Blood|2019Cited by 1