Successful engraftment of gene-corrected hematopoietic stem cells in non-conditioned patients with Fanconi anemiaPaula Rı́o, Juan A. Bueren, María L. Lamana et al.|Nature Medicine|2019Cited by 180
Next-generation Sequencing in Bone Marrow Failure Syndromes and Isolated Cytopenias: Experience of the Spanish Network on Bone Marrow Failure SyndromesEva Heredero Gálvez, Julián Sevilla, Elena Vallespín et al.|HemaSphere|2021Cited by 26
Improved collection of hematopoietic stem cells and progenitors from Fanconi anemia patients for gene therapy purposesJulián Sevilla, Juan A. Bueren, Susana Navarro et al.|Molecular Therapy — Methods & Clinical Development|2021Cited by 25
Advances in the Gene Therapy of Patients with Fanconi AnemiaJuan A. Bueren, Julián Sevilla, Susana Navarro et al.|Blood|2018Cited by 3
Hematopoietic Engraftment of Fanconi Anemia Patients through 3 Years after Gene TherapyPaula Rı́o, Juan A. Bueren, Susana Navarro et al.|Blood|2019Cited by 1