Successful engraftment of gene-corrected hematopoietic stem cells in non-conditioned patients with Fanconi anemiaPaula Rı́o, Juan A. Bueren, Ning Wu et al.|Nature Medicine|2019Cited by 180
Engraftment and in vivo proliferation advantage of gene-corrected mobilized CD34+ cells from Fanconi anemia patientsPaula Rı́o, Juan A. Bueren, Guillermo Güenechea et al.|Blood|2017Cited by 60
Lentiviral-mediated Genetic Correction of Hematopoietic and Mesenchymal Progenitor Cells From Fanconi Anemia PatientsAriana Jacome, Juan A. Bueren, Susana Navarro et al.|Molecular Therapy|2009Cited by 49
Advances in the Gene Therapy of Patients with Fanconi AnemiaJuan A. Bueren, Julián Sevilla, Susana Navarro et al.|Blood|2018Cited by 3