A Serious Adverse Event after Successful Gene Therapy for X-Linked Severe Combined Immunodeficiency

Salima Hacein‐Bey‐Abina(Centre National de la Recherche Scientifique), Alain Fischer(Inserm), N. M. Wulffraat(Centre National de la Recherche Scientifique), Jean‐Luc Villeval(Inserm), Manfred Schmidt(Centre National de la Recherche Scientifique), Christof von Kalle(Luxembourg Institute of Health), Elisabeth McIntyre, Christopher C. Fraser, Marina Cavazzana(Université Rennes 2), Françoise Le Deist(Centre National de la Recherche Scientifique), Isabelle Radford
New England Journal of Medicine
January 15, 2003
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