Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia
Marina Cavazzana(Délégation Paris 5), Philippe Leboulch(Brigham and Women's Hospital), Gèrard Socié(Hôpital Saint-Louis), Stany Chrétien(Inserm), Nabil Kabbara(Université Paris Cité), Frederic D. Bushman(University of Pennsylvania), F. Galactéros(Assistance Publique – Hôpitaux de Paris), Gary Wang(University of Pennsylvania), Alain Fischer(Université Claude Bernard Lyon 1), Laure Caccavelli(Hôpital Necker-Enfants Malades), Françoise Bernaudin(Hôpital Intercommunal de Créteil), Geert-Jan Mulder(Epix Pharmaceuticals (United States)), Béatrix Gillet-Legrand(Commissariat à l'Énergie Atomique et aux Énergies Alternatives), B. Gourmel(Université Paris Cité), Emmanuel Payen(Inserm), Ronald Dorazio(Epix Pharmaceuticals (United States)), Éliane Gluckman(Université Paris Cité), Riccardo Sgarra(University of Trieste), Nathalie Cartier(Commissariat à l'Énergie Atomique et aux Énergies Alternatives), Yves Beuzard(Inserm), Olivier Nègre(Inserm), Floriane Fusil(Inserm), Troy Brady(University of Pennsylvania), Axel Polack(Epix Pharmaceuticals (United States)), Jean Soulier(Centre National de la Recherche Scientifique), Jérôme Larghero(Université Paris Cité), Kathleen Hehir(Epix Pharmaceuticals (United States)), Resy Cavallesco(Brigham and Women's Hospital), Salima Hacein‐Bey‐Abina, Kenneth Cornetta(Indiana University – Purdue University Indianapolis), B Dalle(Université Paris Cité), Maria Denaro(Epix Pharmaceuticals (United States)), Karen A. Westerman(Brigham and Women's Hospital), Arthur Bank(Columbia University), Robert Girot(Sorbonne Université), Julian D. Down(Epix Pharmaceuticals (United States)), Patrick Aubourg(Délégation Paris 5)
Cited by 1,272
Related Papers
Linking Long-Term Dietary Patterns with Gut Microbial Enterotypes
|Science|2011|6.6k
Intestinal microbiota metabolism of l-carnitine, a nutrient in red meat, promotes atherosclerosis
|Nature Medicine|2013|4.4k
<i>LMO2</i> -Associated Clonal T Cell Proliferation in Two Patients after Gene Therapy for SCID-X1
|Science|2003|3.5k
Impaired type I interferon activity and inflammatory responses in severe COVID-19 patients
|Science|2020|3.2k
Gene Therapy of Human Severe Combined Immunodeficiency (SCID)-X1 Disease
|Science|2000|2.6k