Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia
Marina Cavazzana(Université Rennes 2), Philippe Leboulch(Brigham and Women's Hospital), Gèrard Socié(Hôpital Saint-Louis), Stany Chrétien(Hôpital Necker-Enfants Malades), Nabil Kabbara(Université Paris Cité), Frederic D. Bushman(University of Pennsylvania), F. Galactéros(Université Paris-Est Créteil), Gary Wang(Google (United States)), Alain Fischer(Inserm), Laure Caccavelli(Hôpital Necker-Enfants Malades), Françoise Bernaudin(Université Paris-Est Créteil), Geert-Jan Mulder(Epix Pharmaceuticals (United States)), Béatrix Gillet-Legrand(Commissariat à l'Énergie Atomique et aux Énergies Alternatives), B. Gourmel(Université Paris Cité), Emmanuel Payen(Inserm), Ronald Dorazio(Epix Pharmaceuticals (United States)), Éliane Gluckman(Assistance Publique – Hôpitaux de Paris), Riccardo Sgarra(University of Trieste), Nathalie Cartier(Université Paris-Sud), Yves Beuzard(Inserm), Olivier Nègre(Inserm), Floriane Fusil(Inserm), Troy Brady(University of Pennsylvania), Axel Polack(Epix Pharmaceuticals (United States)), Jean Soulier(Centre National de la Recherche Scientifique), Jérôme Larghero(Délégation Paris 5), Kathleen Hehir(Epix Pharmaceuticals (United States)), Resy Cavallesco(Brigham and Women's Hospital), Salima Hacein‐Bey‐Abina(Centre National de la Recherche Scientifique), Kenneth Cornetta(Indiana University – Purdue University Indianapolis), B Dalle(Université Paris Cité), Maria Denaro(Epix Pharmaceuticals (United States)), Karen A. Westerman(Brigham and Women's Hospital), Arthur Bank(Columbia University), Robert Girot(Sorbonne Université), Julian D. Down(Epix Pharmaceuticals (United States)), Patrick Aubourg(Inserm)
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