Successful engraftment of gene-corrected hematopoietic stem cells in non-conditioned patients with Fanconi anemiaPaula Rı́o, Juan A. Bueren, Susana Navarro et al.|Nature Medicine|2019Cited by 180
Haematopoietic gene therapy of non-conditioned patients with Fanconi anaemia-A: results from open-label phase 1/2 (FANCOLEN-1) and long-term clinical trialsPaula Rı́o, Josune Zubicaray, Susana Navarro et al.|The Lancet|2024Cited by 27
Improved collection of hematopoietic stem cells and progenitors from Fanconi anemia patients for gene therapy purposesJulián Sevilla, Juan A. Bueren, Susana Navarro et al.|Molecular Therapy — Methods & Clinical Development|2021Cited by 25
Upregulation of NKG2D ligands impairs hematopoietic stem cell function in Fanconi anemiaJosé Antonio Casado, Juan A. Bueren, Antonio Valeri et al.|Journal of Clinical Investigation|2022Cited by 7
Hematopoietic Engraftment of Fanconi Anemia Patients through 3 Years after Gene TherapyPaula Rı́o, Juan A. Bueren, Susana Navarro et al.|Blood|2019Cited by 1