Hematopoietic Stem Cell Gene Therapy with a Lentiviral Vector in X-Linked Adrenoleukodystrophy
Nathalie Cartier(Université Paris-Sud), Patrick Aubourg(Inserm), Cynthia C. Bartholomae(German Cancer Research Center), Philippe Leboulch(Brigham and Women's Hospital), Alain Fischer(Inserm), Laure Caccavelli(Hôpital Necker-Enfants Malades), Pierre Bougnères(Commissariat à l'Énergie Atomique et aux Énergies Alternatives), Muriel Audit(GenoSafe), Ulrich Abel(German Cancer Research Center), Véronique Kiermer(Public Library of Science), Emmanuel Payen(Inserm), Gábor Veres(Southwest General Health Center), Michel Vidaud(Institut de Soudure), Marina Cavazzana(Université Rennes 2), Nizar Mahlaoui(Hôpital Necker-Enfants Malades), Manfred Schmidt(Centre National de la Recherche Scientifique), Bruno L’Homme(Délégation Paris 5), Liliane Dal‐Cortivo(Hôpital Necker-Enfants Malades), Céline Bellesme(Hôpital Saint-Vincent-de-Paul), Ina Kutschera(German Cancer Research Center), Christof von Kalle(Luxembourg Institute of Health), Salima Hacein‐Bey‐Abina(Centre National de la Recherche Scientifique), Denice Mittelstaedt(Qualcomm (United States)), Najiba Lahlou(Hôpital Saint-Vincent-de-Paul), François Lefrère(Hôpital Necker-Enfants Malades), Stéphane Blanche(Délégation Paris 5)
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