Eteplirsen for the treatment of Duchenne muscular dystrophyJerry R. Mendell, Kim Shontz, Christopher M. Walker et al.|Annals of Neurology|2013Cited by 793
Dystrophin Immunity in Duchenne's Muscular DystrophyJerry R. Mendell, Christopher M. Walker, Katherine Campbell et al.|New England Journal of Medicine|2010Cited by 655
Gentamicin‐induced readthrough of stop codons in duchenne muscular dystrophyVinod Malik, Jerry R. Mendell, Louise R. Rodino‐Klapac et al.|Annals of Neurology|2010Cited by 272
Sustained alpha‐sarcoglycan gene expression after gene transfer in limb‐girdle muscular dystrophy, type 2DJerry R. Mendell, K. Reed Clark, Louise R. Rodino‐Klapac et al.|Annals of Neurology|2010Cited by 243
A Phase 1/2a Follistatin Gene Therapy Trial for Becker Muscular DystrophyJerry R. Mendell, Brian K. Kaspar, Zarife Sahenk et al.|Molecular Therapy|2014Cited by 232