Sustained alpha‐sarcoglycan gene expression after gene transfer in limb‐girdle muscular dystrophy, type 2D
Jerry R. Mendell(Nationwide Children's Hospital), K. Reed Clark(Nationwide Children's Hospital), Julie M. Gastier‐Foster(Nationwide Children's Hospital), Thomas J. Conlon(University of Florida), Zarife Sahenk(The Ohio State University), Janaiah Kota(Ultragenyx Pharmaceutical (United States)), William G. Bremer(Nationwide Children's Hospital), Kevin M. Flanigan(Nationwide Children's Hospital), Christopher M. Walker(University of Kansas Medical Center), Xiomara Q. Rosales(Nationwide Children's Hospital), Sarah Lewis(Nationwide Children's Hospital), Brian D. Coley(Cincinnati Children's Hospital Medical Center), Laura E. Taylor(Nationwide Children's Hospital), Barry J. Byrne(University of Florida), Gloria Galloway(Nationwide Children's Hospital), Vinod Malik(Nationwide Children's Hospital), Chris Shilling(Nationwide Children's Hospital), Louise R. Rodino‐Klapac(Sarepta Therapeutics (United States)), Katherine J. Campbell(Nationwide Children's Hospital), Caroline Astbury
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