Eteplirsen for the treatment of Duchenne muscular dystrophyJerry R. Mendell, Chris Shilling, Kathleen R. Melia et al.|Annals of Neurology|2013Cited by 793
Dystrophin Immunity in Duchenne's Muscular DystrophyJerry R. Mendell, Christopher M. Walker, Katherine Campbell et al.|New England Journal of Medicine|2010Cited by 655
Assessment of Systemic Delivery of rAAVrh74.MHCK7.micro-dystrophin in Children With Duchenne Muscular DystrophyJerry R. Mendell, Louise R. Rodino‐Klapac, Zarife Sahenk et al.|JAMA Neurology|2020Cited by 387
Gentamicin‐induced readthrough of stop codons in duchenne muscular dystrophyVinod Malik, Jerry R. Mendell, Louise R. Rodino‐Klapac et al.|Annals of Neurology|2010Cited by 272
Sustained alpha‐sarcoglycan gene expression after gene transfer in limb‐girdle muscular dystrophy, type 2DJerry R. Mendell, K. Reed Clark, Louise R. Rodino‐Klapac et al.|Annals of Neurology|2010Cited by 243