A Phase 1/2a Follistatin Gene Therapy Trial for Becker Muscular Dystrophy

Jerry R. Mendell(Nationwide Children's Hospital), Brian K. Kaspar(Nationwide Children's Hospital), Zarife Sahenk(The Ohio State University), Katherine Berry(Muscular Dystrophy Association), Eric S. Meadows(Target (United States)), Lindsay N. Alfano(Nationwide Children's Hospital), Kevin M. Flanigan(Nationwide Children's Hospital), Alessandra Govoni(Azienda Ospedaliero-Universitaria Careggi), Ana M. Gómez(Nationwide Children's Hospital), Xiomara Q. Rosales(Nationwide Children's Hospital), Lyndsey Braun(Nationwide Children's Hospital), Sarah Lewis(Nationwide Children's Hospital), Mark Hogan(Nationwide Children's Hospital), Kim Shontz(Nationwide Children's Hospital), K. Reed Clark(Nationwide Children's Hospital), Vinod Malik(Nationwide Children's Hospital), Linda Lowes(Nationwide Children's Hospital), Louise R. Rodino‐Klapac(Sarepta Therapeutics (United States)), Samiah Al-Zaidy(The Ohio State University), Maria Rouhana(Nationwide Children's Hospital)

Molecular Therapy

October 17, 2014

Cited by 232

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