A Phase 1/2a Follistatin Gene Therapy Trial for Becker Muscular Dystrophy
Jerry R. Mendell(Nationwide Children's Hospital), Zarife Sahenk(Nationwide Children's Hospital), Vinod Malik(Nationwide Children's Hospital), Ana M. Gómez(Nationwide Children's Hospital), Kevin M. Flanigan(Nationwide Children's Hospital), Linda Lowes(The Ohio State University), Lindsay N. Alfano(The Ohio State University), Katherine Berry(The Ohio State University), Eric S. Meadows(Nationwide Children's Hospital), Sarah Lewis(Nationwide Children's Hospital), Lyndsey Braun(Nationwide Children's Hospital), Kim Shontz(Nationwide Children's Hospital), Maria Rouhana(Nationwide Children's Hospital), K. Reed Clark(Nationwide Children's Hospital), Xiomara Q. Rosales(Nationwide Children's Hospital), Samiah Al-Zaidy(Nationwide Children's Hospital), Alessandra Govoni(Nationwide Children's Hospital), Louise R. Rodino‐Klapac(Nationwide Children's Hospital), Mark Hogan(Nationwide Children's Hospital), Brian K. Kaspar(Nationwide Children's Hospital)
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