Dystrophin Immunity in Duchenne's Muscular DystrophyJerry R. Mendell, Christopher M. Walker, Chengwen Li et al.|New England Journal of Medicine|2010Cited by 655
Sustained alpha‐sarcoglycan gene expression after gene transfer in limb‐girdle muscular dystrophy, type 2DJerry R. Mendell, K. Reed Clark, Louise R. Rodino‐Klapac et al.|Annals of Neurology|2010Cited by 243
A Phase 1/2a Follistatin Gene Therapy Trial for Becker Muscular DystrophyJerry R. Mendell, Brian K. Kaspar, Zarife Sahenk et al.|Molecular Therapy|2014Cited by 232
Limb‐girdle muscular dystrophy type 2D gene therapy restores α‐sarcoglycan and associated proteinsJerry R. Mendell, K. Reed Clark, Christopher M. Walker et al.|Annals of Neurology|2009Cited by 214