A Serious Adverse Event after Successful Gene Therapy for X-Linked Severe Combined ImmunodeficiencySalima Hacein‐Bey‐Abina, Alain Fischer, Christof von Kalle et al.|New England Journal of Medicine|2003Cited by 1.8k
Insertional oncogenesis in 4 patients after retrovirus-mediated gene therapy of SCID-X1Salima Hacein‐Bey‐Abina, Marina Cavazzana, Alexandrine Garrigue et al.|Journal of Clinical Investigation|2008Cited by 1.8k
Hematopoietic Stem Cell Gene Therapy with a Lentiviral Vector in X-Linked AdrenoleukodystrophyNathalie Cartier, Patrick Aubourg, Salima Hacein‐Bey‐Abina et al.|Science|2009Cited by 1.5k
Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemiaMarina Cavazzana, Philippe Leboulch, Emmanuel Payen et al.|Nature|2010Cited by 1.3k
Sustained Correction of X-Linked Severe Combined Immunodeficiency by ex Vivo Gene TherapySalima Hacein‐Bey‐Abina, Marina Cavazzana, Frédérique Carlier et al.|New England Journal of Medicine|2002Cited by 1.1k