Sustained Correction of X-Linked Severe Combined Immunodeficiency by ex Vivo Gene Therapy
Salima Hacein‐Bey‐Abina, Marina Cavazzana(Délégation Paris 5), Adrian J. Thrasher(Great Ormond Street Hospital), Cécile Bouneaud, Frédérique Carlier, Alain Fischer(Université Claude Bernard Lyon 1), Lilly Leiva, N. M. Wulffraat(Centre National de la Recherche Scientifique), Jean‐Pierre de Villartay(Université Paris Cité), Sophie Dupuis‐Girod
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