Limb‐girdle muscular dystrophy type 2D gene therapy restores α‐sarcoglycan and associated proteins
Jerry R. Mendell(Nationwide Children's Hospital), K. Reed Clark(Nationwide Children's Hospital), Laurence Viollet(Nationwide Children's Hospital), Zarife Sahenk(Nationwide Children's Hospital), Josepha Craenen(Nationwide Children's Hospital), Xiomara Rosales-Quintero(Nationwide Children's Hospital), Janaiah Kota(Indiana University – Purdue University Indianapolis), William G. Bremer(Nationwide Children's Hospital), Christopher M. Walker(Nationwide Children's Hospital), Sarah Lewis(Nationwide Children's Hospital), Brian D. Coley(Nationwide Children's Hospital), Barry J. Byrne(UF Health Shands Hospital), Gloria Galloway(Nationwide Children's Hospital), Vinod Malik(Nationwide Children's Hospital), Katherine J. Campbell(Nationwide Children's Hospital), Louise R. Rodino‐Klapac(Sarepta Therapeutics (United States)), Christopher Shilling(Nationwide Children's Hospital), Thomas J. Conlon(University of Florida)
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