Assessment of Systemic Delivery of rAAVrh74.MHCK7.micro-dystrophin in Children With Duchenne Muscular Dystrophy
Jerry R. Mendell(Nationwide Children's Hospital), Louise R. Rodino‐Klapac(Sarepta Therapeutics (United States)), Zarife Sahenk(Nationwide Children's Hospital), Rachael A. Potter(Nationwide Children's Hospital), C. Nease(Nationwide Children's Hospital), A. Dugar(Sarepta Therapeutics (United States)), M. Iammarino(Nationwide Children's Hospital), Lindsay N. Alfano(Nationwide Children's Hospital), Kelly J. Lehman(Nationwide Children's Hospital), Linda Cripe(The Ohio State University), Sarah Lewis(Nationwide Children's Hospital), Mark Hogan(Nationwide Children's Hospital), Amanda Nicholl(Nationwide Children's Hospital), Richard Shell(The Ohio State University), Linda Lowes(Nationwide Children's Hospital), N. Miller(Nationwide Children's Hospital), Kathleen Church(Nationwide Children's Hospital), Samiah Al-Zaidy(The Ohio State University), Danielle A. Griffin(Nationwide Children's Hospital), Eric R. Pozsgai(Nationwide Children's Hospital)
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