Lentiviral Gene Therapy for Cerebral Adrenoleukodystrophy
Florian Eichler(Harvard University), David A. Williams(Harvard University), Jean‐Hugues Dalle(Inserm), Elizabeth McNeil(Inserm), Adrian J. Thrasher(Great Ormond Street Hospital), Himal L. Thakar(Dana-Farber/Boston Children's Cancer and Blood Disorders Center), Shaun A. Hussain(Inserm), Patricia L. Musolino(Harvard University), Jörn‐Sven Kühl(Charité - Universitätsmedizin Berlin), Satiro De Oliveira(University of California, Los Angeles), Troy C. Lund(University of Minnesota Children's Hospital), Juliana Folloni Fernandes(Hospital das Clínicas da Faculdade de Medicina da Universidade de São Paulo), Nicholas Smith(Inserm), Paul J. Orchard(University of Minnesota), Caroline Sevin(Bicêtre Hospital), Laura A. Demopoulos(Inserm), Raman Sankar(University of California, Los Angeles), Uwe Platzbecker(Cape Town HVTN Immunology Laboratory / Hutchinson Centre Research Institute of South Africa), Ashish O. Gupta(Dana-Farber/Boston Children's Cancer and Blood Disorders Center), Paul Gissen(Great Ormond Street Hospital), Andrew C. Dietz(Dana-Farber/Boston Children's Cancer and Blood Disorders Center), Gerald Downey(Dana-Farber/Boston Children's Cancer and Blood Disorders Center), Christine Duncan(Dana-Farber Cancer Institute), Daniel J. Loes(Inserm), Hernán Amartino(Manchester Royal Eye Hospital), Patrick Aubourg(Délégation Paris 5)
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