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The Changing Face of AdrenoleukodystrophyJia Zhu, Joseph A. Majzoub, Florian Eichler et al.|Endocrine Reviews|2020Cited by 71
Lentiviral Gene Therapy for Cerebral AdrenoleukodystrophyFlorian Eichler, David A. Williams, Christine Duncan et al.|New England Journal of Medicine|2024Cited by 71