Hematologic Cancer after Gene Therapy for Cerebral Adrenoleukodystrophy

Christine Duncan(Dana-Farber/Boston Children's Cancer and Blood Disorders Center), David A. Williams(Boston Children's Hospital), Geoffrey Parsons(Dana-Farber/Boston Children's Cancer and Blood Disorders Center), Vinod K. Prasad(Dana-Farber/Boston Children's Cancer and Blood Disorders Center), Melissa Bonner(Dana-Farber/Boston Children's Cancer and Blood Disorders Center), Marianna Foos(Dana-Farber/Boston Children's Cancer and Blood Disorders Center), Himal L. Thakar(Dana-Farber/Boston Children's Cancer and Blood Disorders Center), Melissa A. Kinney(Dana-Farber/Boston Children's Cancer and Blood Disorders Center), Jörn‐Sven Kühl(Charité - Universitätsmedizin Berlin), Florian Eichler(Harvard University), Bartosz Grzywacz(Dana-Farber/Boston Children's Cancer and Blood Disorders Center), Richard A. Colvin(Dana-Farber/Boston Children's Cancer and Blood Disorders Center), Paul J. Orchard(University of Minnesota), Sarah Slauson(Dana-Farber/Boston Children's Cancer and Blood Disorders Center), Jacob R. Bledsoe(Boston Children's Hospital), Ashish O. Gupta(University of Minnesota), Ankit Lodaya(Dana-Farber/Boston Children's Cancer and Blood Disorders Center), Amy Beckman(Dana-Farber/Boston Children's Cancer and Blood Disorders Center), Andrew C. Dietz(Dana-Farber/Boston Children's Cancer and Blood Disorders Center), Gerald Downey(Dana-Farber/Boston Children's Cancer and Blood Disorders Center), Nicole Floro(Dana-Farber/Boston Children's Cancer and Blood Disorders Center), Marian H. Harris(Boston Children's Hospital), Francis J. Pierciey(Somerville Hospital)
New England Journal of Medicine
October 9, 2024
Cited by 119


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