Hematopoietic Stem-Cell Gene Therapy for Cerebral Adrenoleukodystrophy
Florian Eichler(Harvard University), David A. Williams(Boston Children's Hospital), Adrian J. Thrasher(Great Ormond Street Hospital), Myriam Armant(Dana-Farber/Boston Children's Cancer and Blood Disorders Center), Patricia L. Musolino(Harvard University), Satiro De Oliveira(University of California, Los Angeles), Troy C. Lund(University of Minnesota Medical Center), Nicholas Smith(Women's and Children's Health Network), Paul J. Orchard(University of Minnesota), Caroline Sevin(Bicêtre Hospital), Tara O’Meara, Ami J. Shah(University of California, Los Angeles), H. Bobby Gaspar(University College London), Weston P. Miller(University of Minnesota Children's Hospital), Drago Bratkovic(Women's and Children's Hospital), Colleen Dansereau(Dana-Farber/Boston Children's Cancer and Blood Disorders Center), Asif Paker(Dana-Farber/Boston Children's Cancer and Blood Disorders Center), Paul Gissen(Great Ormond Street Hospital), Esther Shamir(Dana-Farber/Boston Children's Cancer and Blood Disorders Center), David Davidson(Dana-Farber/Boston Children's Cancer and Blood Disorders Center), Christine Duncan(Dana-Farber/Boston Children's Cancer and Blood Disorders Center), Patrick Aubourg(Inserm), Hernán Amartino(Manchester Royal Eye Hospital), Gerald V. Raymond(Kennedy Krieger Institute)
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