Hematopoietic Stem-Cell Gene Therapy for Cerebral Adrenoleukodystrophy
Florian Eichler(Harvard University), David A. Williams(Harvard University), Adrian J. Thrasher(Great Ormond Street Hospital), Myriam Armant(Dana-Farber/Boston Children's Cancer and Blood Disorders Center), Patricia L. Musolino(Harvard University), Satiro De Oliveira(University of California, Los Angeles), Troy C. Lund(University of Minnesota Children's Hospital), Nicholas Smith(Women's and Children's Hospital), Paul J. Orchard(University of Minnesota), Caroline Sevin(Bicêtre Hospital), Tara O’Meara, Ami J. Shah(University of California, Los Angeles), H. Bobby Gaspar(Great Ormond Street Hospital), Weston P. Miller(University of Minnesota Children's Hospital), Drago Bratkovic(Women's and Children's Hospital), Colleen Dansereau(Dana-Farber/Boston Children's Cancer and Blood Disorders Center), Asif Paker(Dana-Farber/Boston Children's Cancer and Blood Disorders Center), Paul Gissen(Great Ormond Street Hospital), Esther Shamir(Dana-Farber/Boston Children's Cancer and Blood Disorders Center), David Davidson(Dana-Farber/Boston Children's Cancer and Blood Disorders Center), Christine Duncan(Dana-Farber Cancer Institute), Patrick Aubourg(Délégation Paris 5), Hernán Amartino(Manchester Royal Eye Hospital), Gerald V. Raymond(Johns Hopkins Medicine)
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