Highly efficient therapeutic gene editing of human hematopoietic stem cells
Yuxuan Wu(Qufu Normal University), Daniel E. Bauer(Broad Institute), Scot A. Wolfe(University of Massachusetts Chan Medical School), Kendell Clement(Broad Institute), Alessandra Biffi(University of Padua), Benjamin P. Roscoe(University of Massachusetts Chan Medical School), David M. Dorfman(Brigham and Women's Hospital), Carlo Brugnara(Harvard University), Mitchel A. Cole(Broad Institute), Chunyan Ren(Broad Institute), Christian Brendel(Broad Institute), Luca Biasco(Institute of Infection and Immunity), Cícera R. Lazzarotto(St. Jude Children's Research Hospital), John Manis(Broad Institute), Jing Zeng(Broad Institute), Kevin Luk(University of Massachusetts Chan Medical School), David A. Williams(Boston Children's Hospital), Cristina Baricordi(Broad Institute), Luca Pinello(Broad Institute), Shengdar Q. Tsai(Harvard University), Pengpeng Liu(University of Massachusetts Chan Medical School), Erica B. Esrick(Broad Institute), Qiuming Yao(Broad Institute), Anne H. Shen(Broad Institute)
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