Highly efficient therapeutic gene editing of human hematopoietic stem cells
Yuxuan Wu(Broad Institute), Jing Zeng(Broad Institute), Benjamin P. Roscoe(University of Massachusetts Chan Medical School), Pengpeng Liu(University of Massachusetts Chan Medical School), Qiuming Yao(Broad Institute), Cícera R. Lazzarotto(St. Jude Children's Research Hospital), Kendell Clement(Broad Institute), Mitchel A. Cole(Broad Institute), Kevin Luk(University of Massachusetts Chan Medical School), Cristina Baricordi(Broad Institute), Anne H. Shen(Broad Institute), Chunyan Ren(Broad Institute), Erica B. Esrick(Broad Institute), John Manis(Broad Institute), David M. Dorfman(Brigham and Women's Hospital), David A. Williams(Broad Institute), Alessandra Biffi(Broad Institute), Carlo Brugnara(Broad Institute), Luca Biasco(Broad Institute), Christian Brendel(Broad Institute), Luca Pinello(Broad Institute), Shengdar Q. Tsai(St. Jude Children's Research Hospital), Scot A. Wolfe(University of Massachusetts Chan Medical School), Daniel E. Bauer(Boston Children's Hospital)
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