Gene Therapy for Fanconi Anemia: One Step Closer to the Clinic
Jakub Tolar(University of Minnesota System), Juan A. Bueren(Centro de Investigación Biomédica en Red), Helmut Hanenberg(Indiana University – Purdue University Indianapolis), Pankaj Qasba(National Institutes of Health), Susana Navarro(Centre for Biomedical Network Research on Rare Diseases), Pamela S. Becker(City Of Hope National Medical Center), D. Wade Clapp(Indiana University School of Medicine), Cristina Díaz de Heredia(Universitat Autònoma de Barcelona), Julián Sevilla(University of Southern Denmark), Manfred Schmidt(Centre National de la Recherche Scientifique), Hans‐Peter Kiem(Fred Hutch Cancer Center), Els Verhoeyen(Université Claude Bernard Lyon 1), Paula Rı́o(Centre for Biomedical Network Research on Rare Diseases), Adrian J. Thrasher(Great Ormond Street Hospital)
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