Long-term enzyme correction and lipid reduction in multiple organs of primary and secondary transplanted Fabry mice receiving transduced bone marrow cellsToshihiro Takenaka, Jeffrey A. Medin, Toshio Ohshima et al.|Proceedings of the National Academy of Sciences|2000Cited by 96
Gene Therapy for Fanconi Anemia: One Step Closer to the ClinicJakub Tolar, Juan A. Bueren, Pamela S. Becker et al.|Human Gene Therapy|2012Cited by 75