Eteplirsen for the treatment of Duchenne muscular dystrophyJerry R. Mendell, A.M. Gomez, Sarah Lewis et al.|Annals of Neurology|2013Cited by 793
Longitudinal effect of eteplirsen versus historical control on ambulation in <scp>D</scp> uchenne muscular dystrophyJerry R. Mendell, Eugenio Mercuri, Nathalie Goemans et al.|Annals of Neurology|2015Cited by 502
Assessment of Systemic Delivery of rAAVrh74.MHCK7.micro-dystrophin in Children With Duchenne Muscular DystrophyJerry R. Mendell, Louise R. Rodino‐Klapac, Zarife Sahenk et al.|JAMA Neurology|2020Cited by 387
A Phase 1/2a Follistatin Gene Therapy Trial for Becker Muscular DystrophyJerry R. Mendell, Brian K. Kaspar, Zarife Sahenk et al.|Molecular Therapy|2014Cited by 232