Analysis of long-term treatment effects of odevixibat on clinical outcomes in children with progressive familial intrahepatic cholestasis in odevixibat clinical studies vs external controls from the NAPPED databaseBettina E. Hansen, Philip Stein, Patryk Lipiński et al.|Journal of Hepatology|2023Cited by 3
P1 Analysis of long-term treatment effects of odevixibat on clinical outcomes in children with progressive familial intrahepatic cholestasis in odevixibat clinical studies vs external controls from the NAPPED databaseBettina E. Hansen, Philip Stein, Velichka Valcheva et al.|Poster presentations|2023Cited by 2
SAT-387 Trajectories of serum bile acid levels and their determinants in progressive familial intrahepatic cholestasis: insights from the NAPPED consortiumP. H. Huisman, Jernej Brecelj, Henkjan J. Verkade et al.|Journal of Hepatology|2025Cited by 0
OS-086 Event-free survival of maralixibat-treated patients with progressive familial intrahepatic cholestasis compared with aligned real-world data of untreated patients from NAPPEDPedro Miranda Afonso, Denitza Kofinova, Alise D. E. de Groot et al.|Journal of Hepatology|2026Cited by 0
THU-284 Missense variants in the ABCB11 gene and disease severity in patients with bile salt export pump deficiencyMark Nomden, Nolwenn Laborde, Alise D. E. de Groot et al.|Journal of Hepatology|2026Cited by 0