OS-086 Event-free survival of maralixibat-treated patients with progressive familial intrahepatic cholestasis compared with aligned real-world data of untreated patients from NAPPED
Pedro Miranda Afonso(Erasmus MC), Denitza Kofinova, Emmanuel Gonzalès(Université Paris-Sud), Loreto Hierro Llanillo, Angelo Di Giorgio(University of Udine), Sandra Ferreira, Andrea Goldstein, Cristina Gonçalves(Hospital de Santa Maria), Alexandre Fabre(Aix-Marseille Université), A Azaz, Girish Gupte, Winita Hardikar(Royal Children's Hospital), Étienne Sokal(Cliniques Universitaires Saint-Luc), Ryan T. Fischer(Children's Mercy Hospital), Agustina Kadaristiana(King's College London), Pier Luigi Calvo(University of Turin), María Belén Pallitto, Marianne Hørby Jørgensen, Jernej Brecelj(University of Ljubljana), Douglas Mogul(Johns Hopkins Medicine), E. Barkaoui, Irena Jankowska(Children's Memorial Health Institute), Carolina Jiménez‐Rivera(Children's Hospital of Eastern Ontario), Paola Mian, Mara Cananzi(University of Padua), Mark Nomden, Marisa Beretta, Alise D. E. de Groot, Cigdem Arikan, Benjamin Shneider, Özlem Durmaz, Elisa de Carvalho, Tassos Grammatikopoulos, Richard J. Thompson, Shannon Vandriel, Kyung Mo Kim, Enke Grabhorn, Emmanuel Jacquemin, Seema Alam, Huey-Ling Chen, Dominique Debray, Guillermo Costaguta, Henrik Arnell, Madeleine Aumar, Wikrom Karnsakul, Björn Fischler, Nanda Kerkar, Giuseppe Indolfi(Meyer Children's Hospital), Antal Dezsőfi-Gottl, Jae Sung Ko(Seoul National University)
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