P1 Analysis of long-term treatment effects of odevixibat on clinical outcomes in children with progressive familial intrahepatic cholestasis in odevixibat clinical studies vs external controls from the NAPPED database

Bettina E. Hansen(Aarhus University), Philip Stein(Yale University), Dieter Broering(King Faisal Specialist Hospital & Research Centre), Déirdre Kelly(Princess Margaret Cancer Centre), Emmanuel Gonzalès(Université Paris-Sud), Esra Polat, Amer Azaz(Shaikh Khalifa Medical City), Özlem Durmaz(Istanbul University), Tassos Grammatikopoulos(King's College London), Björn Fischler(Karolinska University Hospital), Henrik Arnell(Karolinska University Hospital), Jaak Sõnajalg, Daniele Serranti(Università Cattolica del Sacro Cuore), Cristina Gonçalves(Hospital de Santa Maria), Enke Grabhorn(Universität Hamburg), Wendy L. van der Woerd(University Medical Center Utrecht), Étienne Sokal(Cliniques Universitaires Saint-Luc), Emanuele Nicastro(Ospedale Papa Giovanni XXIII), Antonia Felzen(University Medical Center Groningen), Zerrin Önal(Istanbul University), Nathalie Rock(Hôpital de l'enfance), Mohammad Shagrani(Alfaisal University), Agustina Kadaristiana(King's College London), Çiğdem Arıkan(Medizinische Hochschule Hannover), Pier Luigi Calvo(University of Turin), Dominique Debray(Hôpital Necker-Enfants Malades), Piotr Czubkowski(Children's Memorial Health Institute), Jernej Brecelj(University of Ljubljana), Ekkehard Sturm(University Children's Hospital Tübingen), Binita M. Kamath(Children's Hospital of Philadelphia), Loreto Hierro(Hospital Universitario La Paz), Irena Jankowska(Children's Memorial Health Institute), Anne Spraul(Université Paris-Sud), Emmanuel Jacquemin(Inserm), Gabriella Nebbia(Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico), Fowzan S. Alkuraya(Alfaisal University), Florence Lacaille(Hôpital Necker-Enfants Malades), Mark Nomden, Meddirevula Sateesh, Antal Dezs odblac fi(Semmelweis University), Patryk Lipi nacute ski(Children's Memorial Health Institute), Liting Li(Sun Yat-sen University), Qifeng Yu(Northwestern Polytechnical University), Kishwer Kumar, Daan BE van Wessel(University Medical Center Groningen), Yael Mozer‐Glassberg(Schneider Children's Medical Center), Gema Muñoz Bartolo(Hospital Universitario La Paz), Velichka Valcheva, Jian‐She Wang, Richard J. Thompson(King's College London)
Poster presentations
September 1, 2023
Cited by 2


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