Analysis of long-term treatment effects of odevixibat on clinical outcomes in children with progressive familial intrahepatic cholestasis in odevixibat clinical studies vs external controls from the NAPPED database
Bettina E. Hansen(Aarhus University), Philip Stein(Yale University), Emmanuel Gonzalès(Université Paris-Sud), Amer Azaz(Shaikh Khalifa Medical City), Özlem Durmaz(Istanbul University), Tassos Grammatikopoulos(King's College London), Dieter C. Bröering(Universität Hamburg), Björn Fischler(Karolinska University Hospital), Henrik Arnell(Karolinska University Hospital), Patryk Lipiński(Children's Memorial Health Institute), Jaak Sõnajalg, Daniele Serranti(Università Cattolica del Sacro Cuore), Cristina Gonçalves(Hospital de Santa Maria), Daan van Wessel(Vifor Pharma (United States)), Esra Polat(Ümraniye Eğitim ve Araştırma Hastanesi), Enke Grabhorn(Universität Hamburg), Wendy L. van der Woerd(University Medical Center Utrecht), Étienne Sokal(Cliniques Universitaires Saint-Luc), Emanuele Nicastro(Ospedale Papa Giovanni XXIII), Antonia Felzen(University Medical Center Groningen), Zerrin Önal(Istanbul University), Nathalie Rock(Hôpital de l'enfance), Mohammad Shagrani(Alfaisal University), Agustina Kadaristiana(King's College London), Çiğdem Arıkan(Medizinische Hochschule Hannover), Richard Thompson(University of Alberta), Pier Luigi Calvo(University of Turin), Dominique Debray(Hôpital Necker-Enfants Malades), Piotr Czubkowski(Children's Memorial Health Institute), Jernej Brecelj(University of Ljubljana), Ekkehard Sturm(University Children's Hospital Tübingen), Antal Dezsőfi(Semmelweis University), Binita M. Kamath(Children's Hospital of Philadelphia), Irena Jankowska(Children's Memorial Health Institute), Anne Spraul(Université Paris-Sud), Emmanuel Jacquemin(Inserm), Gabriella Nebbia(Fondazione IRCCS Ca' Granda Ospedale Maggiore Policlinico), Fowzan S. Alkuraya(Alfaisal University), Florence Lacaille(Hôpital Necker-Enfants Malades), Mark Nomden, Meddirevula Sateesh, Liting Li(Sun Yat-sen University), Qifeng Yu(Northwestern Polytechnical University), Kishwer Kumar, Yael Mozer‐Glassberg(Schneider Children's Medical Center), Gema Muñoz Bartolo(Hospital Universitario La Paz), Velichka Valcheva, Jian‐She Wang, Déirdre Kelly(Princess Margaret Cancer Centre)
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