In Utero Gene Therapy (IUGT) Using GLOBE Lentiviral Vector Phenotypically Corrects the Heterozygous Humanised Mouse Model and Its Progress Can Be Monitored Using MRI Techniques

Panicos Shangaris(St Thomas' Hospital), Anna L. David(KU Leuven), Paolo De Coppi(Great Ormond Street Hospital), Michael Antoniou(Guy's Hospital), Christina Flouri, Sindhu Subramaniam(University College London), Simon N. Waddington(University College London), Laurence H. Jackson(University College London), Thomas M. Ryan, Luca Urbani(King's College London), Shanrun Liu, Panagiotis Maghsoudlou(University Hospitals Bristol NHS Foundation Trust), Ayad Eddaoudi(University College London), Simon Eaton(Great Ormond Street Hospital), Joy Archer(University of Cambridge), Manfred Schmidt(Centre National de la Recherche Scientifique), Stavros Loukogeorgakis(Queen Mary University of London), Nahla Bakhamis(University College London), Michael P. Blundell(University College London), Wei Wang(Chinese Academy of Sciences), Daniel J. Stuckey(University College London), Durrgah L. Ramachandra(University College London), Adrian J. Thrasher(Great Ormond Street Hospital)
Scientific Reports
August 12, 2019
Cited by 27


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