Sustained transgene expression despite T lymphocyte responses in a clinical trial of rAAV1-AAT gene therapy

Mark Brantly(University of Florida), Terence R. Flotte(University of Massachusetts Chan Medical School), Michael R. Betts(University of Pennsylvania), Roberto Calcedo(Johns Hopkins University), James M. Wilson(St Bartholomew's Hospital), L. Terry Spencer(University of Florida), Margaret Humphries(University of Massachusetts Chan Medical School), Barry J. Byrne(University of Florida), Jeffrey D. Chulay(Research Triangle Park Foundation), Farshid N. Rouhani(University of Florida), Lili Wang(Hunan Agricultural University), Christian Mueller(AbbVie (Germany)), Carolyn Spencer(Boston Children's Hospital), Thomas J. Conlon(Adelson Foundation)
Proceedings of the National Academy of Sciences
August 12, 2009
Cited by 322


Related Papers