MicroRNA-regulated, Systemically Delivered rAAV9: A Step Closer to CNS-restricted Transgene ExpressionJun Xie, Guangping Gao, Hongwei Zhang et al.|Molecular Therapy|2010Cited by 168
Human Treg responses allow sustained recombinant adeno-associated virus–mediated transgene expressionChristian Mueller, Terence R. Flotte|Journal of Clinical Investigation|2013Cited by 160
CRISPR/Cas9-Mediated Excision of ALS/FTD-Causing Hexanucleotide Repeat Expansion in <i>C9ORF72</i> rescues major disease mechanisms <i>in vivo</i> and <i>in vitro</i>Katharina E. Meijboom, Christian Mueller|bioRxiv (Cold Spring Harbor Laboratory)|2022Cited by 1