MicroRNA-regulated, Systemically Delivered rAAV9: A Step Closer to CNS-restricted Transgene Expression
Jun Xie(Hainan University), Guangping Gao(University of Massachusetts Chan Medical School), Phillip D. Zamore(Howard Hughes Medical Institute), Hiroki Kato(University of Bonn), Jui‐Hung Hung(Boston University), Qing Xie(Shanghai Jiao Tong University), Craig C. Mello(University of Massachusetts Chan Medical School), Qin Su, Xin Mu(Nanjing Agricultural University), Stefan L. Ameres(Institute of Molecular Biotechnology), Zhiping Weng(UMass Memorial Health Care), Ran He(Sun Yat-sen University), Hongwei Zhang(University of Massachusetts Chan Medical School), Soyeon Park(Keimyung University), Chengjian Li(Zhengzhou Central Hospital), Christian Mueller(AbbVie (Germany)), Seemin Seher Ahmed(University of Massachusetts Chan Medical School), Terence R. Flotte(University of Massachusetts Chan Medical School)
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