CRISPR/Cas9-Mediated Excision of ALS/FTD-Causing Hexanucleotide Repeat Expansion in <i>C9ORF72</i> rescues major disease mechanisms <i>in vivo</i> and <i>in vitro</i>
Katharina E. Meijboom(University of Massachusetts Chan Medical School), Christian Mueller(University of Massachusetts Chan Medical School)
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