Comparative Studies Reveal Robust HbF Induction By Editing of HBG1/2 Promoters or BCL11A Erythroid-Enhancer in Human CD34+ Cells but That BCL11A Erythroid-Enhancer Editing Is Associated with Selective Reduction in Erythroid Lineage Reconstitution in a Xenotransplantation ModelKai‐Hsin Chang, Haiyan Jiang, Kiran Gogi et al.|Blood|2018Cited by 9
PS1518 GENOME EDITING OF HBG1/2 PROMOTER LEADS TO ROBUST HBF INDUCTION IN VIVO, WHILE EDITING OF BCL11A ERYTHROID ENHANCER RESULTS IN ERYTHROID DEFECTSJonathon Heath, Kaiwen Chang, Edouard De Dreuzy et al.|HemaSphere|2019Cited by 8
Efficient in vivo editing of CEP290 IVS26 by EDIT-101 as a novel therapeutic for treatment of Leber Congenital Amaurosis 10Michael Stefanidakis, Haiyan Jiang, Morgan L. Maeder et al.|Investigative Ophthalmology & Visual Science|2018Cited by 3