PS1518 GENOME EDITING OF HBG1/2 PROMOTER LEADS TO ROBUST HBF INDUCTION IN VIVO, WHILE EDITING OF BCL11A ERYTHROID ENHANCER RESULTS IN ERYTHROID DEFECTS

Jonathon Heath(Editas Medicine (United States)), Kaiwen Chang(Xinxiang Medical University), Gregory Gotta(Editas Medicine (United States)), Ramya Viswanathan(Editas Medicine (United States)), Patricia Sousa(Editas Medicine (United States)), Eugenio Marco(Editas Medicine (United States)), Emily Brennan(Editas Medicine (United States)), Georgia Giannoukos(Editas Medicine (United States)), John A. Zuris(Howard Hughes Medical Institute), Terence Ta(Editas Medicine (United States)), T. Wang(Editas Medicine (United States)), Scott Haskett(Editas Medicine (United States)), Edouard De Dreuzy(Editas Medicine (United States)), Diana Tabbaa(Broad Institute), Charlie Albright(Editas Medicine (United States)), Meltem Isik(Editas Medicine (United States)), Jamaica Siwak(Editas Medicine (United States)), Manuel Sánchez(Universitat de Miguel Hernández d'Elx), Christopher Wilson(Vanderbilt University Medical Center), Fuji Ta(Editas Medicine (United States)), Sérgio Teixeira(Editas Medicine (United States))
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