Efficient in vivo editing of CEP290 IVS26 by EDIT-101 as a novel therapeutic for treatment of Leber Congenital Amaurosis 10

Michael Stefanidakis(Editas Medicine (United States)), Haiyan Jiang(Inner Mongolia Agricultural University), Georgia Giannoukos(Editas Medicine (United States)), Steven J. Samuelsson(Procter & Gamble (United States)), Hoson Chao(Editas Medicine (United States)), Scott Haskett(Editas Medicine (United States)), Pam Stetkiewicz(Editas Medicine (United States)), Christopher J. Wilson, Charlie Albright(Editas Medicine (United States)), Morgan L. Maeder(Editas Medicine (United States)), Delena Nguyen(Editas Medicine (United States)), Peter Baciu(Editas Medicine (United States)), Clifford Yudkoff(Editas Medicine (United States)), Eugenio Marco(Editas Medicine (United States)), Dawn Ciulla(Broad Institute), George S. Bounoutas(Editas Medicine (United States))

Investigative Ophthalmology & Visual Science

July 13, 2018

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