In vivo adenine base editing of PCSK9 in macaques reduces LDL cholesterol levelsTanja Rothgangl, Gerald Schwank, Denis V. Victorov et al.|Nature Biotechnology|2021Cited by 375
In vivo prime editing of a metabolic liver disease in miceDesirée Böck, Gerald Schwank, Tanja Rothgangl et al.|Science Translational Medicine|2022Cited by 184
Treatment of a metabolic liver disease in mice with a transient prime editing approachTanja Rothgangl, Gerald Schwank, András Tálas et al.|Nature Biomedical Engineering|2025Cited by 21
Replacing the SpCas9 HNH domain by deaminases generates compact base editors with an alternative targeting scopeLukas Villiger, Gerald Schwank, Lukas Schmidheini et al.|Molecular Therapy — Nucleic Acids|2021Cited by 21
Treatment of a genetic liver disease in mice through transient prime editor expressionTanja Rothgangl, Gerald Schwank, Eleonora Ioannidi et al.|bioRxiv (Cold Spring Harbor Laboratory)|2024Cited by 4