Treatment of a metabolic liver disease in mice with a transient prime editing approach

Tanja Rothgangl(University of Zurich), Gerald Schwank(University of Zurich), Lukas Schmidheini(University of Zurich), Paulo J.C. Lin(University of British Columbia), Beat Thöny(University of Zurich), Péter István Kulcsár(University of Zurich), Steven H.Y. Fan(Acuitas Therapeutics (Canada)), Johannes Häberle(University Children's Hospital Zurich), Mai Matsushita(ETH Zurich), Nicole Rimann(University Children's Hospital Zurich), Ying K. Tam(Arbutus Biopharma (Canada)), Norbert Pardi(University of Pennsylvania), Alessio Cremonesi(University of Zurich), Yanik Weber(University of Zurich), Hiromi Muramatsu(University of Pennsylvania), András Tálas(University of Zurich), Máté Vadovics(University of Pennsylvania), Erica Faccin(University Children's Hospital Zurich), Manfred Köpf(École Polytechnique Fédérale de Lausanne), Elina Andrea Villiger(University of Zurich), Eleonora I. Ioannidi(University of Zurich), Desirée Böck(University of Zurich), Cornelia Schwerdel(University of Zurich), Lukas Villiger(McGovern Institute for Brain Research), Woohyun J Moon(Acuitas Therapeutics (Canada)), Kim Fabiano Marquart(University of Zurich)
Nature Biomedical Engineering
May 20, 2025
Cited by 21


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