Treatment of a metabolic liver disease in mice with a transient prime editing approach
Tanja Rothgangl(University of Zurich), Gerald Schwank(University of Zurich), Lukas Schmidheini(University of Zurich), Paulo J.C. Lin(University of British Columbia), Péter István Kulcsár(University of Zurich), Johannes Häberle(University Children's Hospital Zurich), Mai Matsushita(ETH Zurich), Nicole Rimann(University Children's Hospital Zurich), Ying K. Tam(Arbutus Biopharma (Canada)), Alessio Cremonesi(University of Zurich), Yanik Weber(University of Zurich), Hiromi Muramatsu(University of Pennsylvania), András Tálas(University of Zurich), Máté Vadovics(University of Pennsylvania), Erica Faccin(University Children's Hospital Zurich), Manfred Köpf(École Polytechnique Fédérale de Lausanne), Elina Andrea Villiger(University of Zurich), Eleonora I. Ioannidi(University of Zurich), Desirée Böck(University of Zurich), Cornelia Schwerdel(University of Zurich), Norbert Pardi, Woohyun J Moon(Acuitas Therapeutics (Canada)), Lukas Villiger(McGovern Institute for Brain Research), Steven H Y Fan, Kim Fabiano Marquart(University of Zurich)
Cited by 0
Related Papers
Rational design of cationic lipids for siRNA delivery
|Nature Biotechnology|2010|1.8k
The Onpattro story and the clinical translation of nanomedicines containing nucleic acid-based drugs
|Nature Nanotechnology|2019|1.6k
Maximizing the Potency of siRNA Lipid Nanoparticles for Hepatic Gene Silencing In Vivo**
|Angewandte Chemie International Edition|2012|1.2k
CAR T Cells Produced in vivo to Treat Cardiac Injury
|HAL (Le Centre pour la Communication Scientifique Directe)|2023|940