The Onpattro story and the clinical translation of nanomedicines containing nucleic acid-based drugs

Akin Akinc(Alnylam Pharmaceuticals (United States)), Pieter R. Cullis(University of British Columbia), Barbara L. Mui(Arbutus Biopharma (Canada)), Xinyao Du(Acuitas Therapeutics (Canada)), Sean C. Semple(Arbutus Biopharma (Canada)), Dominik Witzigmann(FPInnovations), Muthusamy Jayaraman(Alnylam Pharmaceuticals (United States)), Roy van der Meel(Eindhoven University of Technology), Ying K. Tam(Arbutus Biopharma (Canada)), Martin A. Maier(Alnylam Pharmaceuticals (United States)), Marco A. Ciufolini(FPInnovations), Muthiah Manoharan(Alnylam Pharmaceuticals (United States)), Michael J. Hope(Acuitas Therapeutics (Canada)), Steven M. Ansell(Acuitas Therapeutics (Canada)), Kevin Fitzgerald(Epsilon Systems (United States)), Jayesh A. Kulkarni(University of British Columbia), Thomas D. Madden(Arbutus Biopharma (Canada)), Scott Barros(Alnylam Pharmaceuticals (United States))
Nature Nanotechnology
December 1, 2019
Cited by 1,559


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