Non-neurological, non-skeletal outcomes after hematopoietic stem and progenitor cell-gene therapy (OTL-203) for Hurler syndrome
Francesca Tucci(Vita-Salute San Raffaele University), Maria Ester Bernardo(Unknown), Chiara Filisetti(Vita-Salute San Raffaele University), Michele Colombo(Vita-Salute San Raffaele University), Maurizio De Pellegrin(IRCCS Ospedale San Raffaele), Stefania Galimberti(University of Milano-Bicocca), Giulia Danè(Vita-Salute San Raffaele University), Maria Pia Manitto(Vita-Salute San Raffaele University), Silvia Darin(The San Raffaele Telethon Institute for Gene Therapy), Giulia Risca(University of Milano-Bicocca), Stefano Scarparo(The San Raffaele Telethon Institute for Gene Therapy), María Luz Uria Oficialdegui(Vall d'Hebron Hospital Universitari), Alessandro Aiuti(University of Rome Tor Vergata), Cristina Díaz de Heredia(Universitat Autònoma de Barcelona), Elisabetta Martina(Vita-Salute San Raffaele University), Sonia Bonanomi(Azienda Ospedaliera San Gerardo), Chiara Camesasca(IRCCS Ospedale San Raffaele), Marina Sarzana(Vita-Salute San Raffaele University), Paolo Silvani(Istituto di Ricovero e Cura a Carattere Scientifico San Raffaele), Serena Gasperini(Azienda Ospedaliera San Gerardo), Giulia Consiglieri(University of Rome Tor Vergata), Roberto Santangelo(Vita-Salute San Raffaele University), Luigi Naldini(Vita-Salute San Raffaele University), Rossella Parini(MRC Epidemiology Unit), Mireia del Toro(Universitat Autònoma de Barcelona), Francesca Fumagalli(Vita-Salute San Raffaele University), Carla Butera(Vita-Salute San Raffaele University), Bernhard Gentner(The San Raffaele Telethon Institute for Gene Therapy), Monica Stoppani(Vita-Salute San Raffaele University), Matilde Cossutta(The San Raffaele Telethon Institute for Gene Therapy)
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