Intersecting impact of CAG repeat and huntingtin knockout in stem cell-derived cortical neurons

Jennifer Stocksdale(University of California, Irvine), Leslie M. Thompson(University of California, Irvine), Kanchan Sarda(Gladstone Institutes), Terry T.‐K. Huang(The Graduate Center, CUNY), Dan P. Felsenfeld(CHDI Foundation), Niveda Sundararaman(Cedars-Sinai Medical Center), Yuxin Xu(Harvard University), Zohreh Faghihmonzavi(Gladstone Institutes), Ernest Fraenkel(Massachusetts Institute of Technology), Jie Wu(University of California, Irvine), Ricardo Miramontes(University of California, Irvine), Keona Q. Wang(University of California, Irvine), Steven Finkbeiner(Gladstone Institutes), Stephanie Lam(Gladstone Institutes), Julia Kaye(Gladstone Institutes), Min‐Gyoung Shin(Gladstone Institutes), Vineet Vaibhav(Cedars-Sinai Medical Center), Yi Wang(Cedars-Sinai Medical Center), Thomas Vogt(CHDI Foundation), Charlene Smith(University of California, Irvine), Mariya Barch(Gladstone Institutes), Chris Paiz(Gladstone Institutes), Lindsay Easter(Gladstone Institutes), Erse Duderstadt(Gladstone Institutes), Matthew Leventhal(Broad Institute), Yogi Raghav(Massachusetts Institute of Technology), Jennifer E. Van Eyk(Cedars-Sinai Smidt Heart Institute)
Neurobiology of Disease
April 19, 2025
Cited by 4


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