20861. GIVINOSTAT EN DISTROFIA MUSCULAR DE DUCHENNE: COMPARACIÓN DE HISTORIA NATURAL APLICANDO PUNTUACIÓN DE PROPENSIÓN
C. McDonald, Stefano Cazzaniga(University of Verona), Mariacristina Scoto(University College London), K. Vandenborne, Tracey Willis(Robert Jones and Agnes Hunt Orthopaedic Hospital), N. Coceani(Italfarmaco (Italy)), P. Bettica(Italfarmaco (Italy)), H. Phan(Rare Disease Therapeutics (United States)), Valeria Sansone(University of Milan), M. Michela
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