Safety and efficacy of givinostat in boys with Duchenne muscular dystrophy (EPIDYS): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trialEugenio Mercuri, A. Nascimento, Wolfgang Müller‐Felber et al.|The Lancet Neurology|2024Cited by 128
429P Givinostat in Duchenne muscular dystrophy: natural history comparison applying propensity score matchingC. McDonald, Valeria Sansone, H. Phan et al.|Neuromuscular Disorders|2024Cited by 1
20861. GIVINOSTAT EN DISTROFIA MUSCULAR DE DUCHENNE: COMPARACIÓN DE HISTORIA NATURAL APLICANDO PUNTUACIÓN DE PROPENSIÓNC. McDonald, Valeria Sansone, H. Phan et al.|Neurology Perspectives|2024Cited by 0
Givinostat in Duchenne Muscular Dystrophy: Natural history comparison applying propensity score matchingDavid Gómez‐Andrés, P. Bettica, Mercedes López Lobato et al.|Nervenheilkunde|2025Cited by 0