Safety and efficacy of givinostat in boys with Duchenne muscular dystrophy (EPIDYS): a multicentre, randomised, double-blind, placebo-controlled, phase 3 trial
Eugenio Mercuri(Università Cattolica del Sacro Cuore), A. Nascimento(Centre for Biomedical Network Research on Rare Diseases), Francina Munell(Vall d'Hebron Institut de Recerca), Migvis Monduy, Craig M. Zaidman(Washington University in St. Louis), E. Niks(Leiden University Medical Center), Laura McAdam, Giovanni Baranello, Stefan Spinty(Alder Hey Children's NHS Foundation Trust), Odile Boespflug‐Tanguy(Inserm), Claudia Brogna(Università Campus Bio-Medico), Mercedes López Lobato, Imelda J. M. de Groot(Duchenne Parent Project), John F. Brandsema, Sara Cazzaniga(Italfarmaco (Italy)), Kevin Carroll(Cheshire West and Chester), Francesca Magri, Krista Vandenborne(University of Florida), Wolfgang Müller‐Felber(Ludwig-Maximilians-Universität München), Giacomo P. Comi(University of Milan), Kathryn Selby(University of British Columbia), Ulrike Schara‐Schmidt(University of Duisburg-Essen), Sonia Messina(University of Messina), Liesbeth De Waele(KU Leuven), Chamindra G. Laverty(University of California San Diego), Nathalie Goemans, Teresa Gidaro(Center for Neurosciences), Astrid Blaschek(Ludwig-Maximilians-Universität München), Jessika Johannsen(Universität Hamburg), Gyula Acsádi(Connecticut Children's Medical Center), Enrico Bertini(Bambino Gesù Children's Hospital), Laurent Servais(University of Oxford), Craig M. McDonald(University of California Davis Medical Center), Giulia Zardi, Barry J. Byrne(University of Florida), Erika Finanger, Juan J. Vílchez(Universitat de València), Richard S. Finkel(St. Jude Children's Research Hospital), N. Coceani(Italfarmaco (Italy)), Jean K. Mah(University of Calgary), P. Bettica(Italfarmaco (Italy)), Anne M. Connolly(Washington University in St. Louis), Georgios Manousakis, Nuria Muelas Gómez, Marcos Madruga Garrido, Claudio Bruno(Istituto Giannina Gaslini), M. Guglieri, Amy Harper, Riccardo Masson
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