Precise CRISPR-Cas9 gene repair in autologous memory T cells to treat familial hemophagocytic lymphohistiocytosis

Xun Li(Max Delbrück Center), Klaus Rajewsky(Max Delbrück Center), Ingo Müller(Universität Hamburg), Thomas Sommermann(Max Delbrück Center), Andreas Zach(Max Delbrück Center), Elijah D. Lowenstein(Beth Israel Deaconess Medical Center), Kathrin de la Rosa(Max Delbrück Center), Johannes H. Schulte(German Cancer Research Center), Tristan Wirtz(Max Delbrück Center), Timm Weber(University of Cologne), Mikhail Lebedin(Max Delbrück Center), Christine Kocks(Max Delbrück Center), Tomoharu Yasuda(Hiroshima University), Van Trung Chu(The State Bank of Vietnam)
Science Immunology
February 2, 2024
Cited by 13


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