Using a novel measuring device to objectively evaluate the clinical benefit on ptosis in infantile-onset Pompe disease (IOPD): Results from 145 weeks' avalglucosidase alfa dosing in Mini-COMET participants previously treated with alglucosidase alfa
Priya S. Kishnani(Duke Medical Center), S. Grace Prakalapakorn(Duke University), James Davison(Great Ormond Street Hospital for Children NHS Foundation Trust), Satoko Kumada(Tokyo Metropolitan Neurological Hospital), Swathi Tammireddy, Marguerite C. Weinert, Kristina An Haack(Sanofi (France)), Alexander Broomfield(St Mary's Hospital), Hirotaka Ohki(Tokyo Metropolitan Children's Medical Center), Olivier Huynh‐Ba(Sanofi (France)), Susan Sparks(Children's National), Anaïs Brassier(Hôpital Necker-Enfants Malades), Tianyue Zhou, David Kronn(New York Medical College), Yin‐Hsiu Chien(National Taiwan University Hospital), François Labarthe(Université de Tours), Sihoun Hahn(Mayo Clinic)
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