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The Mini-COMET Clinical Trial: Safety and Efficacy of Avalglucosidase Alfa after 97 Weeks of Treatment in Children with Infantile-Onset Pompe Disease Previously Treated with Alglucosidase AlfaDavid Kronn, James Davison, Alexander Broomfield et al.|The Journal of Pediatrics|2025Cited by 3
Mini-COMET: Individual-level treatment responses in infantile-onset Pompe disease participants receiving avalglucosidase alfa or alglucosidase alfa who previously received alglucosidase alfaPriya S. Kishnani, David Kronn, Alexander Broomfield et al.|Molecular Genetics and Metabolism|2021Cited by 1
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