Clinical outcomes after long-term treatment with alglucosidase alfa in infants and children with advanced Pompe disease
Marc Nicolino(Université Claude Bernard Lyon 1), Priya S. Kishnani(Duke Medical Center), John-Charles A. Loo(MemorialCare Long Beach Medical Center), Alison Skrinar, B. Chabrol(Hôpital d'Enfants), Georgianne L. Arnold(University of Rochester Medical Center), Deeksha Bali(MRC Epidemiology Unit), Barry J. Byrne(University of Florida), Shigemi Kimura(Kumamoto University), David R. Freyer(University of Southern California), C. J. Ottinger(FWRadiology), Hanna Mandel(Rebecca Sieff Hospital), Claire Morgan(AstraZeneca (United States)), Luciano Tatò(University of Verona), Shawn E. McCandless(University Hospitals of Cleveland), Nancy Leslie(Cincinnati Children's Hospital Medical Center), Philip Jardine(Bristol Royal Hospital for Children), Lakshmi Mehta(Schneider Children's Hospital), Martin Smitka(Technische Universität Dresden), Enikö K. Pivnick(University of Tennessee Health Science Center), J. Edmund Wraith(Royal Manchester Children's Hospital), Deya Corzo(Millennium Engineering and Integration (United States)), Lakshmi Rangachari
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