Clinical outcomes after long-term treatment with alglucosidase alfa in infants and children with advanced Pompe disease
Marc Nicolino(Université Claude Bernard Lyon 1), Barry J. Byrne(UF Health Shands Hospital), J. Edmund Wraith(Royal Manchester Children's Hospital), Nancy Leslie(Cincinnati Children's Hospital Medical Center), Hanna Mandel(Rambam Health Care Campus), David R. Freyer(Spectrum Health), Georgianne L. Arnold(University of Rochester Medical Center), Enikö K. Pivnick(University of Tennessee Health Science Center), C. J. Ottinger(FWRadiology), Peter H. Robinson(Royal Hospital for Children), John-Charles A. Loo(MemorialCare Long Beach Medical Center), Martin Smitka(Technische Universität Dresden), Philip Jardine(Bristol Royal Hospital for Children), Luciano Tatò(University of Verona), B. Chabrol(Aix-Marseille Université), Shawn E. McCandless(University Hospitals of Cleveland), Shigemi Kimura(Kumamoto University), Lakshmi Mehta(Mount Sinai Medical Center), Deeksha Bali(Duke University), Alison Skrinar, Claire Morgan, Lakshmi Rangachari, Deya Corzo(Millennium Engineering and Integration (United States)), Priya S. Kishnani(Duke University)
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